Gain of Toxicity from ALS/FTD-Linked Repeat Expansions in C9ORF72 Is Alleviated by Antisense Oligonucleotides Targeting GGGGCC-Containing RNAs
University of California San Diego · Ludwig Cancer Research · +14 more institutions
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Abstract
No abstract available for this paper.
Citation impact
537
total citations
- FWCI
- 42.11
- Percentile
- 100%
- References
- 69
Citations per year
Authors
41- JJJie Jiang
University of California San Diego, Ludwig Cancer Research
- QZQiang Zhu
University of California San Diego, Ludwig Cancer Research
- TFTania F. Gendron
Mayo Clinic in Florida
- SSShahram Saberi
University of California San Diego
- MMMelissa McAlonis‐Downes
University of California San Diego, Ludwig Cancer Research
Topics & keywords
Topics
Keywords
- C9orf72
- Amyotrophic lateral sclerosis
- Trinucleotide repeat expansion
- Frontotemporal dementia
- Antisense RNA
- RNA
- Biology
- Oligonucleotide
No related works found for this paper.
Funding
- JHJohns Hopkins University
- LILudwig Institute for Cancer Research
- TATarget ALS
- IPIonis Pharmaceuticals
- ECEuropean CommissionAward: 617198
- FWFonds Wetenschappelijk Onderzoek
- VRVlaamse regering
- NINational Institutes of HealthAwards: T32 AG00216, NS084974, NS077402, NS084528, NS089979, NS087227, NS063964
- UOUniversity of California, San Diego
- MRMedical Research CouncilAward: MR/L021803/1
- RPRobert Packard Center for ALS Research, Johns Hopkins University