reviewMolecular Therapy — Methods & Clinical DevelopmentDec 1, 2017GOLD OA

Emerging Issues in AAV-Mediated In Vivo Gene Therapy

PCPasqualina ColellaGRGiuseppe RonzittiFMFederico Mingozzi

Inserm · Genethon (France) · +3 more institutions

PubMed
Indexed incrossrefdoajpubmed

Abstract

Applications, and present key achievements and emerging issues in the field. We will use the liver as a model target tissue for gene transfer based on the large amount of data available from preclinical and clinical studies.

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Authors

3

Topics & keywords

Topics
Keywords
  • Genetic enhancement
  • In vivo
  • Computational biology
  • Biology
  • Medicine
  • Gene
  • Genetics
UN Sustainable Development Goals
  • Good health and well-being
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