article·Nature Medicine·Mar 25, 2019Closed access

Highly efficient therapeutic gene editing of human hematopoietic stem cells

YWYuxuan WuCorresponding authorJZJing ZengBPBenjamin P. RoscoePLPengpeng LiuQYQiuming Yao

Broad Institute · Boston Children's Hospital · +13 more institutions

PubMed
Indexed incrossrefpubmed

Abstract

No abstract available for this paper.

Citation impact

515
total citations
FWCI
25.38
Percentile
100%
References
48
Citations per year

Authors

24
  • YW
    Yuxuan WuCorresponding

    Broad Institute, Boston Children's Hospital, Harvard University, Dana-Farber Cancer Institute, Harvard Stem Cell Institute, East China Normal University

  • JZ
    Jing Zeng

    Broad Institute, Boston Children's Hospital, Harvard University, Dana-Farber Cancer Institute, Harvard Stem Cell Institute

  • BP
    Benjamin P. Roscoe

    University of Massachusetts Chan Medical School

  • PL
    Pengpeng Liu

    University of Massachusetts Chan Medical School

  • QY
    Qiuming Yao

    Broad Institute, Boston Children's Hospital, Harvard University, Massachusetts General Hospital, Dana-Farber Cancer Institute, Center for Cancer Research, Harvard Stem Cell Institute

Topics & keywords

Topics
  • Primary topicCRISPR and Genetic Engineering100%
  • Hemoglobinopathies and Related Disorders100%
  • Prenatal Screening and Diagnostics95%
Keywords
  • Fetal hemoglobin
  • Cas9
  • Stem cell
  • Biology
  • Haematopoiesis
  • Enhancer
  • Genome editing
  • GATA1
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