Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Università Cattolica del Sacro Cuore · Agostino Gemelli University Polyclinic · +40 more institutions
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Abstract
No abstract available for this paper.
Citation impact
114
total citations
- FWCI
- 23.71
- Percentile
- 100%
- References
- 50
Citations per year
Authors
57- EMEugenio MercuriCorresponding
Università Cattolica del Sacro Cuore, Agostino Gemelli University Polyclinic, Centro Clinico Nemo
- JJJuan J. Vílchez
Hospital Universitari i Politècnic La Fe, Centro de Investigación Biomédica en Red
- OBOdile Boespflug‐Tanguy
Inserm, Université Paris Cité, Sorbonne Université, Hôpital Armand-Trousseau, Assistance Publique – Hôpitaux de Paris, Institut de Myologie, Hôpital Robert-Debré
- CMCraig M. Zaidman
Washington University in St. Louis
- JKJean K. Mah
University of Calgary, Alberta Children's Hospital
Topics & keywords
Topics
Keywords
- Duchenne muscular dystrophy
- Medicine
- Muscular dystrophy
- Placebo
- Dystrophin
- Physical therapy
- Pediatrics
- Internal medicine
UN Sustainable Development Goals
- Good health and well-being
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