reviewMolecular Therapy — Nucleic AcidsSep 26, 2024GOLD OA

CRISPR-Cas9-mediated homology-directed repair for precise gene editing

Sichuan University · West China Second University Hospital of Sichuan University · +1 more institution

PubMed
Indexed incrossrefdoajpubmed

Abstract

Gene therapies. Finally, we discuss alternative precise editing platforms and their limitations, and describe potential avenues to improving CRISPR-Cas9-mediated HDR efficiency and fidelity in future research.

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