In vivo base editing gene therapy for heterozygous familial hypercholesterolemia: a phase 1 trial
Shanghai Jiao Tong University · Renji Hospital · +6 more institutions
Indexed incrossrefpubmed
Abstract
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Citation impact
5
total citations
- FWCI
- 76.09
- Percentile
- 100%
- References
- 39
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Authors
16- PWPing Wan
Shanghai Jiao Tong University, Renji Hospital, Shanghai Genon Biological Products (China)
- STSiyuan Tang
Shanghai Jiao Tong University, Renji Hospital
- DLDongni Lin
Shanghai Jiao Tong University, Renji Hospital
- YLYuming Lu
Shanghai Jiao Tong University, ShanghaiTech University
- MLMei Long
Shanghai Jiao Tong University, Renji Hospital
Topics & keywords
Topics
Keywords
- Familial hypercholesterolemia
- PCSK9
- In vivo
- Genetic enhancement
- Adverse effect
- Clinical trial
- Cholesterol
- Genome editing
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